Bjursell, Mikael, Michelle J. Porritt, Elke Ericson, Amir Taheri-Ghahfarokhi, Maryam Clausen, Lisa Magnusson, Therese Admyre, et al. “Therapeutic CRISPR Cas9 Genome Editing in a Humanized Mouse Model Ameliorates \(\alpha\)1-Antitrypsin Deficiency Phenotype”. Research Perspectives of Microbiology and Biotechnology Vol. 9 (January 25, 2025): 14–31. Accessed June 4, 2026. https://stm.bookpi.org/RPMAB-V9/article/view/16958.